There is a simple discount patient access scheme for vamorolone. NHS organisations can get details on the Commercial Access and Pricing (CAP) Portal. Non-NHS organisations can contact ...

Dystrophy is any condition in which a part of the body weakens or wastes away. In muscular dystrophy, the weakness is in the muscles. An inherited genetic mistake prevents the body from making a ...

In early animal studies and registered human clinical trials in India, Funderburgh and colleagues demonstrated that human corneal stromal stem cells (CSSCs) can regenerate in vitro, and when ...

Clinical features of herpes stromal keratitis Herpes stromal keratitis (HSK) is the most common cause of infectious corneal blindness in developed countries, with most cases resulting from ...

offering new pathways for understanding and treating Duchenne Muscular Dystrophy (DMD). DMD, a severe genetic disorder that causes muscle weakness and shortens lifespans, arises from mutations in ...

Percheron announced on December 18 that its phase 2b trial of its lead candidate avicursen (ATL-1102) into non-ambulant (unable to walk unassisted) boys with Duchenne muscular dystrophy failed to ...

Dec. 16, 2024 — A novel drug holds promise for treating Duchenne muscular dystrophy (DMD), a rare genetic disorder that causes severe muscle degeneration. Researchers have discovered that an ...

Standards and guidelines for development co-operation with concrete examples of their implementation ...