Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) today announced that the U.S. Food and Drug Administration (FDA) has ...

The FDA has granted fast track designation to DYNE-101, a therapy for myotonic dystrophy type 1 (DM1) now in testing in a ...

The way you pay for things is going to need to keep up. Here are some of the best credit cards for young adults, whether you’re totally new to using them, or you’re looking for something a ...

PGN-EDODM1 is under clinical development by Pepgen and currently in Phase I for Myotonic Dystrophy. According to GlobalData, Phase I drugs for Myotonic Dystrophy does not have sufficient historical ...

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Dawes added: "Today, this starts to change." "As age checks start to roll out in the coming months, adults will start to notice a difference in how they access certain online services. Services which ...

The investigational therapy DYNE-101 worked as expected and led to functional improvements for people with myotonic dystrophy type 1 (DM1 ... vein dosing regimens of DYNE-101 against a placebo in ...

There is a simple discount patient access scheme for vamorolone. NHS organisations can get details on the Commercial Access and Pricing (CAP) Portal. Non-NHS organisations can contact ...

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The first to unmask all of its opponents’ spies wins. “This is my favorite party game when mixing kids and adults,” says Scott Cooper, owner of Seattle-based Blue Highway Games. A cross ...

The symptoms of myotonic dystrophy may be obvious from birth or they can develop later -- during the teenage or adult years. Like other forms of muscular dystrophy, myotonic dystrophy leads to ...

Muscular dystrophy can appear in infancy up to middle age or later, and its form and severity are determined in part by the age at which it occurs. Some types of muscular dystrophy typically ...