'My Gaucher Disease Symptoms Were Dismissed As IBS Or Swallowing Air—Here's What Doctors Missed'
The hematology specialist officially diagnosed me with Gaucher disease. The bone marrow biopsy confirmed my diagnosis of ...
Medindia12y
Medications and Drugs for Treatment of Gaucher’s Disease
Find effective medications for 'Gaucher’s Disease treatment right here!' This page is a trusted source for both professionals and patients, detailing brand-name and generic options designed to ...
pharmaphorum7y
NICE recommends Sanofi's Gaucher treatment
England’s NHS will routinely fund Sanofi/Genzyme’s Cerdelga (eliglustat) for the rare condition Gaucher disease after a recommendation from NICE. The cost effectiveness body published final ...
Spur Therapeutics Announces Platform and Poster Presentations Highlighting New Clinical Data for FLT201 in Gaucher Disease at Upcoming WORLDSymposium
Additional details on the meeting can be found at the WORLD Symposium website. About Spur Therapeutics Spur Therapeutics is a clinical-stage biotechnology company focused on developing life-changing ...
pharmaphorum3y
Sanofi's venglustat bombs again, but isn't dead yet
Sanofi is still running studies of the glycosphingolipid (GSL) inhibitor in rare lysosomal storage diseases like Gaucher disease type 3, Fabry disease and GM2 gangliosidosis (also known as Tay ...
Nature2y
Gene-Based Therapeutic Approaches
and congenital neurogenic diabetes insipidus), and lysosomal storage disorders (Gaucher's disease type I, Fabry disease, mucopolysaccharidosis I, mucopolysaccharidosis II, mucopolysaccharidosis VI ...
Pharmabiz10d
NIMHANS hosts ISHG meet to foster innovation for domestic and global healthcare solutions
NIMHANS hosts ISHG meet to foster innovation for domestic and global healthcare solutions: Our Bureau, Bengaluru Tuesday, January 21, 2025, 10:00 Hrs [IST] National Institute of M ...