Truist has initiated coverage of Larimar Therapeutics (NASDAQ:LRMR) with a buy rating, citing an "asymmetric" risk/reward ahead of regulatory updates for its drug candidate nomla for Friedreich’s ...

During the pathogenesis of Parkinson’s disease (PD), α-synuclein pathology may originate in peripheral organs and spread to the CNS. Using human tissue samples and multiple approaches in mouse ...

Initiation of Phase 1b study using SGT-212 for the treatment of patients with Friedreich's Ataxia expected in 2H25. Click ...

Rakovina Therapeutics Inc., a biopharmaceutical company dedicated to advancing new cancer therapies based on novel DNA-damage response technologies, announced the successful achievement of a shortlist ...

Brits have been urged to check this list featuring more than 100 diagnoses, as failing to declare certain medical conditions ...

We searched the PubMed, Cochrane Central Register of Controlled Trials ... with relevant keywords such as “cerebellum,” “spinocerebellar degeneration,” “ataxia,” “physiotherapy,” and “rehabilitation.” ...

The genesis of this program stemmed from our long term commitment to the FA community and our close relationship with the Friedreich's Ataxia Research ... and direct central nervous system ...

Friedreich's Ataxia [FA] is a disorder characterized as ... This article is published by Terry Chrisomalis, who runs the Biotech Analysis Central pharmaceutical service on Seeking Alpha Marketplace.

Using a polymerase chain reaction single strand conformation polymorphism (PCR-SSCP) assay, which amplifies individually all coding exons of the ATM gene deficient ataxia-telangiectasia (A-T), we ...

Methods The authors performed sequencing of known Coenzyme Q10 (CoQ10) deficiency genes in 22 patients with unexplained recessive or sporadic ataxia. Results CABC1/ADCK3 mutations were detected in ...