John Brandsema, MD, a pediatric neurologist at Children’s Hospital of Philadelphia, speaks with Healio about the importance of a smooth transition from pediatric to adult care for patients with ...

When actor Eric Dane revealed his diagnosis of amyotrophic lateral sclerosis (ALS), the world took notice. Novant Health neurologist Dr. Michael Verenes said this has been happening with this ...

Upon approval, vamorolone would be the first and only treatment option indicated for patients diagnosed with Duchenne muscular dystrophy in Canada The Canadian regulatory submission of vamorolone ...

More information: Dariusz C. Górecki et al, Is dystrophin immunogenicity a barrier to advancing gene therapy for Duchenne muscular dystrophy? Gene Therapy (2025). DOI: 10.1038/s41434-025-00531-y ...

ELEVIDYS is indicated for the treatment of Duchenne muscular dystrophy (DMD) in individuals at least 4 years of age. For patients who are ambulatory and have a confirmed mutation in the DMD gene For ...

Few rigorous studies have examined biologic drugs as first-line treatment in adult-onset Still's disease. Results from this cohort study showed that biologics were much more effective than ...

Researchers at Cleveland Clinic have developed a model to predict the risk for colorectal cancer in adults aged younger ... but the rates of early-onset CRC are rising, especially among people ...

He also has limb girdle muscular dystrophy (LGMD), a rare ... The money raised from the event will go to Muscular Dystrophy UK, the leading charity for more than 110,000 adults and children in the UK ...

New research led by the University of Portsmouth has revealed how Duchenne muscular dystrophy (DMD), best known for causing severe muscle degeneration, also profoundly affects the brain ...

Entertainment: West Philly honors Will Smith with street name near his alma mater To benefit Muscular Dystrophy Association (MDA), the Grand Rapids Police Department and the Grand Rapids Fire ...