On this episode, an infant with a harrowing diagnosis defies all odds after receiving a $2 million genetic treatment. Then, a ...
Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...
Nurul Amirah, who lives in Kampung Gaung, Tendong, said all three of her children are diagnosed with spinal muscular atrophy ...
Three patients with spinal muscular atrophy had improved muscle strength and could walk farther after a month of daily spinal stimulation.
About Evrysdi Evrysdi is an SMN2-splicing modifier designed to increase functional SMN protein production. With the introduction of a new tablet formulation, Evrysdi now offers an alternative ...
Daily electrical stimulation of certain nerves in the spinal cord appeared to help three people with spinal muscular atrophy (SMA), an inherited disorder that causes muscles to waste away.
Three patients with spinal muscular atrophy had improved muscle strength and could walk farther after a month of daily spinal stimulation. Spinal stimulation restored muscles wasted by rare ...
An experimental treatment that stimulates the spinal cord may help people with a paralyzing genetic disorder ... when he was diagnosed with spinal muscular atrophy, or SMA, a disorder that ...
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