The symptoms of myotonic dystrophy may be obvious from birth or they can develop later -- during the teenage or adult years. Like other forms of muscular dystrophy, myotonic dystrophy leads to ...

“There are more than 100,000 adults with DM1 in the US and Europe ... ARTHEx also has ATX-01 in preclinical testing for myotonic dystrophy type 2 (DM2). “Although DM2 is caused by a different ...

The FDA has granted fast-track designation to an investigational antisense oligonucleotide to treat individuals with myotonic dystrophy type 1, or DM1, according to the manufacturer. In a press ...

More information: Zachary Dewald et al, Altered drug metabolism and increased susceptibility to fatty liver disease in a ...

We also investigate the pathogenic mechanisms of myotonic dystrophy, type 1 (DM1), an autosomal dominant ... in which failure to express adult splicing patterns causes primary features of the disease.

(RTTNews) - Dyne Therapeutics, Inc. (DYN) Friday announced encouraging data from its ongoing Phase 1/2 ACHIEVE trial of DYNE-101 in patients with myotonic dystrophy type 1 (DM1). Myotonic ...

Jeffrey Donald Carcic, age 62, passed away due to complications of Adult-Onset Myotonic Muscular Dystrophy late in the evening on Tuesday, January 7, 2025. He was born on February 13, 1962 ...