Data from untreated participants were pooled from literature reviews of case series and reports, and a retrospective chart review study. Subgroups were stratified by age of TK2d symptom onset ...

Johnny Mathis recently confirmed that he is stepping back from performing on stage due to problems linked to his age and memory ... Cancer Society and Muscular Dystrophy Association.

One of the most popular music festivals in small-town Illinois is coming to an end after a 10-year run. SamJam’s Finale is scheduled for April 26 in Girard.

New research led by the University of Portsmouth has revealed how Duchenne muscular dystrophy (DMD), best known for causing ...

Becker muscular dystrophy (BMD) is a type of muscular dystrophy, a genetic condition that weakens and damages muscles. It can worsen with age. However, its symptoms are less severe than those of ...

WASHINGTON (AP) — Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for muscular dystrophy, sending company shares plummeting more than 25%.

Results were presented at the 2025 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference. At dosing, microdystrophin expression was 122.3% higher in a patient age three compared to ...

Duchenne Muscular Dystrophy is a genetic disorder characterised ... It can begin as early as age 2 or 3, first affecting the proximal muscles and later affecting the distal limb muscles ...

CAMBRIDGE, Mass., April 04, 2025--(BUSINESS WIRE)--Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, shared the following update related to ...