DMD was first described by French neurologist Guillaume Benjamin Amand Duchenne in the 1860s. However, until the 1980s, ...

Becker muscular dystrophy (BMD) is a type of muscular dystrophy, a genetic condition that weakens and damages muscles. It can worsen with age. However, its symptoms are less severe than those of ...

Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, shared the following ...

Results were presented at the 2025 Muscular Dystrophy Association (MDA ... The new data from the age 1-3 cohort builds on the favorable safety and efficacy profile seen in ages 4 and older ...

Results were presented at the 2025 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference. At dosing, microdystrophin expression was 122.3% higher in a patient age three compared to ...

The data presented at the 2025 Muscular Dystrophy Association Clinical & Scientific ... and transduction levels observed across all treated age groups. The trial is currently enrolling ambulatory ...