Gene therapy developer CRISPR Therapeutics AG (CRSP) is navigating some regulatory and commercial dynamics. Its flagship gene ...

AMT-130 is administered through magnetic resonance imaging-guided, convection-enhanced stereotactic neurosurgical delivery into the striatum.

It's been nearly two years since Elevidys, a gene therapy for Duchenne MD developed by Sarepta Therapeutics, was approved by ...

Novel CAR design selectively targets malignant cells for patients with relapsed/refractory CD5-positive hematological diseasesHOUSTON, April 22, ...

Benjamin K. Chen, MD, PhD, discussed the next steps after the results of his study in genetic tagging showed promise in ...

Approvals for Hemgenix were backed by data from the HOPE-B study that tested a single dose in people with severe hemophilia B ...

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Lila is a Science Writer at BioNews. She completed her PhD in neuroscience at the University of Washington, where she studied ...