'My Gaucher Disease Symptoms Were Dismissed As IBS Or Swallowing Air—Here's What Doctors Missed'
The hematology specialist officially diagnosed me with Gaucher disease. The bone marrow biopsy confirmed my diagnosis of ...
Hosted on MSN1mon
Spur Therapeutics to begin Phase III gene therapy trial in Gaucher disease
Spur Therapeutics has announced that its gene therapy candidate for Gaucher disease will soon be moving to a Phase III trial after positive early data from a Phase I/II trial. Spur, which is a ...
pharmaphorum7y
NICE recommends Sanofi's Gaucher treatment
England’s NHS will routinely fund Sanofi/Genzyme’s Cerdelga (eliglustat) for the rare condition Gaucher disease after a recommendation from NICE. The cost effectiveness body published final ...
Nature1mon
Pfizer stakes a claim in plant cell–made biopharmaceuticals
It acquired rights to taligurase alfa, a form of the enzyme glucocerebrosidase in development for the treatment of Gaucher's disease, from Protalix Biotherapeutics in Carmiel, Israel. Protalix has ...