A cutting-edge gene therapy has been approved for NHS use for some patients with severe sickle cell disease. Casgevy, also ...
Learn about dermatomyositis and the remarkable journey of Audrey Gouskos. Discover how St. Michael's Hospital has provided lifesaving support for her rare disease.
Sanofi SNY reported fourth-quarter 2024 adjusted earnings of 70 cents per American depositary share, which missed the Zacks Consensus Estimate of 71 cents per share. Earnings of €1.31 per share ...
According to the open letter, the delay in rolling out the proposed ₹ 974 crore national programme on rare diseases has exacerbated these challenges, leaving patients, most of whom are children, in ...
Patient advocacy groups warned that delays in implementing India's rare disease policy have left many, including children, in ...
Two new PET radiotracers have outperformed the only current Food and Drug Administration (FDA) approved radiotracer for ...
Ozempic, the blockbuster GLP-1 drug that was originally approved to treat type 2 diabetes, has now also been approved by the ...