The only drug that treats children with a rare degenerative disease called Batten disease could be withdrawn within the next ...

Nicole died from complications linked to it in 2023, while Jessica, nine, still receives a life-prolonging treatment, but the decision whether to keep the drug, Brineura, on the NHS has been ...

The benefits of Biomarin’s Brineura for a very rare inherited condition do not justify its price of more than £520,000 per year, NICE has said in first draft guidance. NICE had been assessing ...

Which Market Leaders Have Staked a Claim in the Brineura Market? The brineura market is served by several key industry players, with major companies including BioMarin Pharmaceutical Inc. leading the ...