Duchenne muscular dystrophy (DMD) is the most common type ... Because DMD can cause heart problems, it's important for your child to see a heart doctor, called a cardiologist, for checkups ...

Although often considered to be diseases of childhood, adult forms of muscular dystrophy occur and represent a spectrum of disease ... of symptoms of congestive heart failure.

Riding recent momentum in the Duchenne muscular dystrophy space, Capricor Therapeutics, Wave Life Sciences, Regenxbio and ...

But with such screening, why hasn't the disease allele frequency gone down? Scientists have been searching for ways to cure DMD for as long as they have known about the disease. Today, based on ...

While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...

The gene therapy improved motor functions in children with Duchenne muscular dystrophy two years after treatment ...

Muscular Dystrophy (MD) is a genetic condition causing progressive muscle weakness and complications in vital organs. Early ...

offering new pathways for understanding and treating Duchenne Muscular Dystrophy (DMD). DMD, a severe genetic disorder that causes muscle weakness and shortens lifespans, arises from mutations in ...

What looks like leg muscle is actually fibrous scarring and fatty replacement from broken-down tissues, a sign of the disease that was making Mason weaker – Duchenne muscular dystrophy — a ...

Objectives: To quantify the magnitude of altruism value as applied to a hypothetical new treatment for a rare, severe pediatric disease: Duchenne muscular dystrophy (DMD). Study Design ...

The announcement was made at Arab Health 2025 where Sidra Medicine will highlight its international patient service programmes ...

Muscular dystrophy ... to treat Duchenne MD. It's only prescribed to people who have a confirmed mutation in the DMD gene. It delivers a protein to muscles in the skeleton, heart, and lungs ...