Despite the obstacles, Riley Herrera had a life filled with family, sports, travel, faith and hope before his death on Nov.
Cumberland Pharmaceuticals’ Duchenne muscular dystrophy (DMD) drug has improved the amount of blood pumped by the heart, ...
Some muscular dystrophies are mild. Others are more serious and can cause life-threatening muscle weakness. Most children with Duchenne muscular dystrophy ... weakness in the shoulders, upper ...
Contrary to prior data, this study shows that neither eosinophils nor STAT6-mediated IL-4/IL-13 signaling contribute ...
Muscular dystrophy is caused by defects in certain genes, with type determined by the abnormal gene. In 1986, researchers discovered the gene that, when defective or flawed, causes Duchenne ...
While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...
Duchenne Muscular Dystrophy (DMD) is a rare progressive disorder. People with DMD are missing muscle-protecting protein. This is due to a fault in the gene producing dystrophin. Muscles to become ...
Sarepta Therapeutics has decided not to continue the development of vesleteplirsen, a follow-up to its Duchenne muscular dystrophy (DMD) therapy Exondys 51. The drug – formerly known as SRP-5051 ...