Duchenne muscular dystrophy (DMD) is the most common type ... They should see a cardiologist in their late teens or early adult years to check for any problem. Some blood pressure medicines ...
Most children with Duchenne muscular dystrophy will need a wheelchair to ... birth or they can develop later -- during the teenage or adult years. Like other forms of muscular dystrophy, myotonic ...
While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...
(RTTNews) - Sarepta Therapeutics, Inc. (SRPT) Monday reported positive topline results from Part 2 of the Phase 3 study, dubbed EMBARK, of its gene therapy Elevidys approved for the treatment of ...
offering new pathways for understanding and treating Duchenne Muscular Dystrophy (DMD). A groundbreaking study has shed light on the complex interactions between dystrophin, a protein critical to ...
The results suggest that prolonging ambulation may not adversely impact cardiac function in adulthood for patients with Duchenne muscular dystrophy (DMD).
A pilot study in 19 LGMD patients and one with Becker MD found low-dose prednisone helped lower markers of muscle damage and ...
Duchenne muscular dystrophy (DMD). Study Design: Prospective survey of individuals not planning to have children in the future. Methods: A survey was administered to US adults (aged ≥ 21 years ...
WASHINGTON, Jan. 15, 2025 /PRNewswire/ -- Parent Project Muscular Dystrophy (PPMD), a nonprofit organization leading the fight to end Duchenne muscular dystrophy (Duchenne), will host its sixth in ...
This mid-stage trial recruited a total of 40 adults and 29 adolescents who ... Speaking of which, the global Duchenne Muscular Dystrophy market is expected to reach $7.4 billion by 2034.