A trial found magnetic resonance imaging correlated with physical function tests in patients with Duchenne muscular dystrophy ...

A major trial of a promising gene therapy for Duchenne muscular dystrophy has fallen short, but researchers say the lessons learned could pave the way for better, more effective treatments.

Two dose levels of a single-administration gene therapy were well-tolerated and led to functional improvements in ambulatory ...

We might expect that for an X-linked lethal recessive disorder (e.g. Duchenne Muscular Dystrophy ... light on how the underlying genetic defect leads to diverse congenital anomalies and ...

An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment. Colton Belluzzo was diagnosed with a form of muscular dystrophy when ...

INDIANAPOLIS (WISH) – Kyle Albertson, an FFA alumnus and Purdue University graduate, shared how FFA prepared him for a career in business despite having congenital muscular dystrophy.

An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment. Colton Belluzzo was diagnosed with a form of muscular dystrophy when ...