Difficulty balancing or an inability to do so can be caused by any number of factors. Head injuries, migraines, alcohol use, ear infections and medications can all affect your musculoskeletal ...
Cerebellar ataxia is a neurological disorder of the cerebellum. This important area at the back of the brain acts as a ...
Only dual route gene transfer therapy in development to treat Friedreich’s ataxia with FDA IND clearance and Fast Track designation ...
Adolescents receive a weight-based dose equivalent to the 50 mg adult dose Adolescents 12-17 years old who complete participation in the ...
Fragile X-Associated Tremor/Ataxia Syndrome (FXTAS) is a neurodegenerative disorder that primarily affects male carriers of the FMR1 gene premutation, characterized by an expansion of CGG ...
Fast-track status will allow Solid Biosciences to have more frequent meetings with the FDA throughout the treatment-development process and, potentially, get the product to patients faster than would ...
The last time I wrote about Larimar Therapeutics, Inc. (NASDAQ:LRMR) it was in a Seeking Alpha article entitled "Larimar: Stronger Buy Now More Than Ever After Partial Clinical Hold Completely ...
Larimar doses adolescents in nomlabofusp paediatric pharmacokinetic run-in study for patients with Friedreich’s ataxia: Bala Cynwyd, Pennsylvania Saturday, January 25, 2025, 15: ...